Correction of genetic disease by making sense from nonsense

J Clin Invest. 1999 Aug;104(4):367-8. doi: 10.1172/JCI8055.
No abstract available

Publication types

  • Comment
  • Review

MeSH terms

  • Animals
  • Codon, Nonsense / drug effects*
  • Dystrophin / genetics
  • Genetic Diseases, Inborn / genetics*
  • Genetic Diseases, Inborn / metabolism
  • Genetic Diseases, Inborn / therapy*
  • Genetic Therapy
  • Gentamicins / metabolism
  • Gentamicins / pharmacology
  • Humans
  • Mice
  • Mice, Inbred mdx
  • Muscular Dystrophy, Animal / drug therapy
  • Muscular Dystrophy, Animal / genetics
  • Muscular Dystrophy, Animal / metabolism
  • Mutation
  • RNA, Messenger / genetics
  • RNA, Messenger / metabolism

Substances

  • Codon, Nonsense
  • Dystrophin
  • Gentamicins
  • RNA, Messenger