No abstract available
MeSH terms
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Animals
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Enzyme Replacement Therapy*
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Gene Expression
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Genetic Diseases, Inborn / therapy*
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Genetic Therapy / methods*
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Humans
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Marfan Syndrome / genetics
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Marfan Syndrome / therapy
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Mutation
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Progeria / genetics
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Progeria / therapy
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Proteins / genetics
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RNA Precursors / metabolism
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RNA Splicing